Drug

Gaboxadol

As of the edition of 20 October 2026, Gaboxadol is a small molecule: stopped in 2021; acts on GABRA4.

Sources: FDA Orange Book and Purple Book, other approval registers, ClinicalTrials.gov, ChEMBL.

The drug

Status
Stopped, 2021
Kind
Small molecule
Registered trials
19, 3 stopped early
Disease areas
Nervous system; Mental health; Inherited and neonatal

US protection

No US approval on record.

With no US approval on record there are no listed US patents or exclusivities.

This is the US only.

Companies that need a new molecule because of this drug

2 companies on route A because of this drug.

Companies on route A for this drug

In the product

2 companies are on route A because of Gaboxadol.

Target

GeneProteinUniProt
GABRA4Gamma-aminobutyric acid receptor subunit alpha-4P48169

Registered trials

PhaseTrialsCompletedActiveStopped early
Phase 11100
Phase 25500
Phase 3131003
All trials19

Who ran its trials

CompanyRoleYears
LundbeckLead sponsor of trials2003 to now
Healx AILead sponsor of trials2016 to now