Drug

Vatiquinone

As of the edition of 20 October 2026, Vatiquinone is a small molecule: in active development; acts on NQO1.

Sources: FDA Orange Book and Purple Book, other approval registers, ClinicalTrials.gov, ChEMBL.

The drug

Status
Active, 2027
Kind
Small molecule
Registered trials
15, 3 stopped early
Disease areas
Nutrition and metabolism; Nervous system; Inherited and neonatal; Bones, joints and muscles; Heart and blood vessels; Immune system

US protection

No US approval on record.

With no US approval on record there are no listed US patents or exclusivities.

This is the US only.

Companies that need a new molecule because of this drug

1 company on route A because of this drug.

Companies on route A for this drug

In the product

1 company is on route A because of Vatiquinone.

Target

GeneProteinUniProt
NQO1NADP15559

Registered trials

PhaseTrialsCompletedActiveStopped early
Phase not stated3000
Phase 11100
Phase 26402
Phase 35221
All trials15

Who ran its trials

CompanyRoleYears
PTC TherapeuticsLead sponsor of trials2014 to now
Edison PharmaceuticalsLead sponsor of trials