Target

BCL11A

BCL11 transcription factor A

As of the edition of 20 October 2026, BCL11A (BCL11 transcription factor A, UniProt Q9H165) has 1 drug tested at it and 1 company on the list, 0 on route A and 1 on route B.

Sources: UniProt, ClinicalTrials.gov, ChEMBL, FDA Orange Book and Purple Book, Pharos.

The protein

UniProt
Q9H165
How well studied
Biology documented; no tool compounds or approved drug yet
Where it sits in the cell
Inside the cell
Solved structures
17
Disease areas
Blood and lymph; Inherited and neonatal; Nutrition and metabolism; Pregnancy and women's health; Urinary and reproductive
Registered trials of its drugs
8

Drugs at this target

StatusCount
Marketed1
Total1
DrugStatusFurthest phaseUS protection
Exagamglogene autotemcelMarketedPhase 3Ends 2035

1 of 1 drugs, the most tested first.

Companies at this target

Where the company standsCompanies
Route B1
Total on the list1
Three companies on route A or B, with the route only
CompanyRoute
VertexRoute B

The other 0 companies at BCL11A

In the product

1 company in all; 0 are not named here, and no score is.

See the 1 companies at BCL11A, ranked, with the facts behind eachRequest access. Nothing is shown until you do.