Target

CEP290

Centrosomal protein of 290 kDa

As of the edition of 20 October 2026, CEP290 (centrosomal protein of 290 kDa, UniProt O15078) has 1 drug tested at it and 2 companies on the list, 1 on route A and 0 on route B.

Sources: UniProt, ClinicalTrials.gov, ChEMBL, FDA Orange Book and Purple Book, Pharos.

The protein

UniProt
O15078
How well studied
Biology documented; no tool compounds or approved drug yet
Where it sits in the cell
Inside the cell
Disease areas
Eye; Inherited and neonatal; Nervous system; Nutrition and metabolism
Registered trials of its drugs
4

Drugs at this target

StatusCount
Stopped1
Total1
DrugStatusFurthest phaseUS protection
SepofarsenStoppedPhase 3none listed

1 of 1 drugs, the most tested first.

Companies at this target

Where the company standsCompanies
Route A1
Engaged1
Total on the list2
Three companies on route A or B, with the route only
CompanyRoute
Laboratoires TheaRoute A

The other 1 company at CEP290

In the product

2 companies in all; 1 is not named here, and no score is.

See the 2 companies at CEP290, ranked, with the facts behind eachRequest access. Nothing is shown until you do.